NEW YORK (Reuters Health) – A new compound, NU-9, improved diseased upper motor neurons (UMN) in mice and shows promise for treating amyotrophic lateral sclerosis (ALS) in humans, though more work is needed before a clinical trial can be started, researchers say. “We identified the first compound that can improve the health of UMNs that […]
The Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency (EMA) has recommended marketing authorization for risdiplam (Evrysdi), the first treatment that can be given orally to patients with certain types of spinal muscular atrophy (SMA). Risdiplam is “expected to increase survival of motor neurons and reduce symptoms of the disease,” […]
